Ionis Pharmaceuticals, Inc.

ionis.com

Total trials

116

Active

22

Phase 3

24

Total enrollment

13,570

Read this sponsor's pipeline like an analyst.

Generate a written report: strategic focus, priority programs, pipeline shape, recent terminations and momentum, and the trials worth watching in the next 12 months.

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Pipeline matrix

Showing 13 of 13 active programs · click any cell for trials

InterventionEarly Phase 1Phase 1Phase 2Phase 3Phase 4N/ATotal
Eplontersen5
Olezarsen10
ION5822
Donidalorsen7
ION3631
zilganersen2
sapablursen2
ION3371
ION7171
ION7751
ION4401
ION3561
ION4641

Next readouts

  • 2025-06-26
  • 2025-08-22
  • 2026-04
  • 2026-06
  • 2026-12
  • 2027-02
  • 2027-03
  • 2027-06
  • 2027-08
  • 2027-09

Top conditions

  • Type 2 Diabetes Mellitus10
  • Hypertriglyceridemia6
  • Hereditary Angioedema5
  • Healthy Volunteers5
  • Severe Hypertriglyceridemia5
  • Familial Chylomicronemia Syndrome5
  • Healthy Participants4
  • Cytomegalovirus Retinitis4

Frequently asked questions about Ionis Pharmaceuticals, Inc.

How many clinical trials does Ionis Pharmaceuticals, Inc. have on ClinicalTrials.gov?
Ionis Pharmaceuticals, Inc. is listed as the lead sponsor on 116 clinical trials in ClinicalTrials.gov, 22 of which are currently active (recruiting, enrolling, or ongoing).
How many of Ionis Pharmaceuticals, Inc.'s trials are in Phase 3?
24 of Ionis Pharmaceuticals, Inc.'s trials are in Phase 3, spread across 13 active drug programs.
What therapeutic areas does Ionis Pharmaceuticals, Inc. focus on?
Ionis Pharmaceuticals, Inc.'s most-studied conditions on ClinicalTrials.gov are Type 2 Diabetes Mellitus, Hypertriglyceridemia, Hereditary Angioedema, Healthy Volunteers, Severe Hypertriglyceridemia.
When are Ionis Pharmaceuticals, Inc.'s next clinical trial readouts?
Ionis Pharmaceuticals, Inc. has 10 upcoming primary-completion readouts tracked here; the soonest is “A Study to Evaluate Sapablursen (Formerly ISIS 702843, IONIS-TMPRSS6-LRx) in Patients With Polycythemia Vera”, expected around 2025-06-26.