Alexion Pharmaceuticals, Inc.

alexion.com

Live pipeline data from ClinicalTrials.gov, refreshed daily.

Total trials

253

Active

42

Phase 3

60

Total enrollment

40,313

Pipeline matrix

Showing 23 of 23 active programs · click any cell for trials

InterventionEarly Phase 1Phase 1Phase 2Phase 3Phase 4N/ATotal
Ravulizumab—31
Acoramidis————2
Prednisone/Prednisolone—————1
Danicopan——22
ALXN1850————4
CAEL-101————3
cyclophosphamide, bortezomib, and Dexamethasone (CyBorD) regimen—————2
asfotase alfa—14
Gefurulimab————2
ALXN1720————2
eneboparatide—————1
ALXN2220—————1
Eculizumab——37
ALXN2030————2
ALXN1920————2
ALXN2420—————1
AZD0120—————1
Tarperprumig—————1
ALXN2350—————1
ALXN2230—————1
Soliris/Ultomiris—————1
hLB-001—————1
Ultomiris—————1

Next readouts

  • 2024-11-15
  • 2025-04-08
  • 2025-05-10
  • 2025-05-27
  • 2025-07-09
  • 2025-07-23
  • 2025-10-09
  • 2026-01-05
  • 2026-01-06
  • 2026-06-22

Top conditions

  • Healthy47
  • Paroxysmal Nocturnal Hemoglobinuria18
  • Hypophosphatasia16
  • Lysosomal Acid Lipase Deficiency12
  • Wilson Disease10
  • Generalized Myasthenia Gravis10
  • PNH8
  • Neuromyelitis Optica Spectrum Disorder7

Frequently asked questions about Alexion Pharmaceuticals, Inc.

How many clinical trials does Alexion Pharmaceuticals, Inc. have on ClinicalTrials.gov?
Alexion Pharmaceuticals, Inc. is listed as the lead sponsor on 253 clinical trials in ClinicalTrials.gov, 42 of which are currently active (recruiting, enrolling, or ongoing).
How many of Alexion Pharmaceuticals, Inc.'s trials are in Phase 3?
60 of Alexion Pharmaceuticals, Inc.'s trials are in Phase 3, spread across 23 active drug programs.
What therapeutic areas does Alexion Pharmaceuticals, Inc. focus on?
Alexion Pharmaceuticals, Inc.'s most-studied conditions on ClinicalTrials.gov are Healthy, Paroxysmal Nocturnal Hemoglobinuria, Hypophosphatasia, Lysosomal Acid Lipase Deficiency, Wilson Disease.
When are Alexion Pharmaceuticals, Inc.'s next clinical trial readouts?
Alexion Pharmaceuticals, Inc. has 10 upcoming primary-completion readouts tracked here; the soonest is “Evaluation of the Safety and Efficacy of Eneboparatide (AZP-3601) in Patients With Chronic Hypoparathyroidism”, expected around 2024-11-15.